Research in action!

Moorfields to begin LCA4 gene therapy

Following promising laboratory experiments, UCL Institute of Ophthalmology and Moorfields Eye Hospital plan to soon be investigating gene therapy with the hope of improving the sight of children affected by a rare inherited eye disease.

The gene therapy, which will initially be administered to a handful of children, could potentially allow children with Leber congenital amourosis type 4 (LCA4) to gain vision.